Exa-cel is the first FDA-approved therapy utilizing CRISPR/Cas9, a type of gene editing technology through which patients' ...

Vertex Pharmaceuticals said on Saturday its gene therapy helped children aged between 5 and 11 years with sickle cell disease ...

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

Casgevy, now a "national priority" drug, helped kids with sickle cell and thalassemia, results which may help toward a label ...

Four decades have passed since cochlear implants gave infants born deaf the ability to hear. Now, gene therapy promises to ...

As a child and family psychologist, I often hear from parents who are struggling with how to approach the subject of therapy with their children. Whether they’re 5 or 15, the thought of saying, “We’re ...

Founded by Kevin Bansely with a commitment to empower school-bound children who face learning complications, this educational ...