A single-dose gene replacement therapy is found to improve movement ability in children over 2 years of age and teenagers ...

Four decades have passed since cochlear implants gave infants born deaf the ability to hear. Now, gene therapy promises to ...

In medicine these days, the word "gene" shows up in all sorts of different contexts and conjugations. There's genetics, of course, and there's genomics. Then there's meta-genomics -- and don't forget ...

A California toddler is the first person in the world to receive gene therapy to treat his devastating disease. Three-year-old Oliver Chu was born with a rare, genetic condition called Hunter syndrome ...

The FDA approved Itvisma gene therapy for patients aged 2 years and older with spinal muscular atrophy and confirmed SMN1 ...

Three years after introducing Hemgenix, the first gene therapy for hemophilia B, CSL Behring has released long-term data ...

Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain.

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

The search for gene therapies to treat rheumatoid arthritis (RA) has moved in fits and starts over the past two decades, with trials starting and stopping, and their focus shifting to osteoarthritis ...

Biotechs in the charter city of Próspera aim to cure aging, but experts question the feasibility of their goals.

Two years ago, he was diagnosed with a terminal illness called Batten disease -- often leading to blindness, seizures, and ...

Regeneron is adding its name to Tessera Therapeutics’ unique in vivo gene writing program, inking a deal that lets it in on a ...