As a parent with a child who has sickle cell disease, you are always on high alert. The “what if” stays with me, as it ...

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

Casgevy, now a "national priority" drug, helped kids with sickle cell and thalassemia, results which may help toward a label ...

LOS ANGELES — Children with sickle cell anemia are vulnerable to serious infections and stroke, but many do not receive the preventive care that could help them stay healthier longer, according to a ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced data from multiple studies demonstrating the clinical benefits of CASGEVY ® (exagamglogene autotemcel) in people ages 5 years and ...

Mary Warlo has been extremely worried lately. Her baby Calieb, who is six months old, has sickle cell disease. In early December he went for a few days without liquid penicillin, a medication that he ...

Exa-cel is the first FDA-approved therapy utilizing CRISPR/Cas9, a type of gene editing technology through which patients' ...

Uganda is among the countries with the highest burden of the disease, with an estimated 33,000 babies born each year carrying the sickle cell trait or disease ...

Less than a third of ED visits for acute sickle cell disease pain were guideline-adherent for the timely administration of ...

Dear Doctor, I am negative, and she is positive, so I had another test, which proved that she did not have sickle cell disease, and so we went ahead and got married.

The guidelines also differ in the follow-up assessment of patients while they are in the emergency room. The NHLBI also recommends reassessing patients every 15 to 30 minutes and readministering pain ...