Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

As a parent with a child who has sickle cell disease, you are always on high alert. The “what if” stays with me, as it ...

Casgevy, now a "national priority" drug, helped kids with sickle cell and thalassemia, results which may help toward a label ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced data from multiple studies demonstrating the clinical benefits of CASGEVY ® (exagamglogene autotemcel) in people ages 5 years and ...

LOS ANGELES — Children with sickle cell anemia are vulnerable to serious infections and stroke, but many do not receive the preventive care that could help them stay healthier longer, according to a ...

Acute kidney injury (AKI) was found to be common in children aged 17 years and younger who were hospitalized for sickle cell anemia. Sickle cell anemia and acute kidney injury (AKI) were found to have ...

Mary Warlo has been extremely worried lately. Her baby Calieb, who is six months old, has sickle cell disease. In early December he went for a few days without liquid penicillin, a medication that he ...

Please provide your email address to receive an email when new articles are posted on . Many children with sickle cell anemia do not receive guideline-concordant preventive care to reduce their risks ...

Less than a third of ED visits for acute sickle cell disease pain were guideline-adherent for the timely administration of ...

Dear Doctor, I am negative, and she is positive, so I had another test, which proved that she did not have sickle cell disease, and so we went ahead and got married.

Uganda is among the countries with the highest burden of the disease, with an estimated 33,000 babies born each year carrying the sickle cell trait or disease. For thousands of families across Uganda, ...