The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...
Kids and teenagers with spinal muscular atrophy had more mobility after receiving a single-dose gene replacement therapy, ...
The chief medical officer of Genetix Biotherapeutics, formerly known as Bluebird bio, discusses timelines and operational ...
The U.S. Food and Drug Administration said on Tuesday it had approved the first gene therapy for a rare and life-threatening ...
Pharmaceutical Technology on MSN
In a Honduran city, biotechs create gene therapy cocktails to fight aging
Biotechs in the charter city of Próspera aim to cure aging, but experts question the feasibility of their goals.
Vence L. Bonham Jr., Acting Deputy Director at the National Human Genome Research Institute (NHGRI) and an investigator in the National Human Genome Research Institute’s (NHGRI) Division of Intramural ...
Hemophilia gene therapies arrived a few years ago with blockbuster expectations. But now, one therapy has been pulled from ...
In October 2025, Karolinska Institutet launched a brand-new two-week course giving PhD students a unique insight into how ...
Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. The New York pharma is ending global development and commercialization of Beqvez ...
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