The rate of severe infections decreased from 2 infections to 0.2 infections per PYO after treatment with etuvetidigene autotemcel.
A new wave of gene therapy treatments offer a new lease on life for people with inherited diseases such as haemophilia. But ...
Doctors in the United Kingdom developed a groundbreaking new gene therapy that is giving hope to patients with aggressive ...
Backed by Italy-based Fondazione Telethon ETS, Waskyra, for Wiskott-Aldrich syndrome, is the first gene therapy from a ...
A groundbreaking gene therapy, BE-CAR7, has shown remarkable success in reversing an aggressive form of leukemia. This ...
Doctors in the UK have developed a groundbreaking gene therapy using base editing to treat aggressive blood cancers once ...
The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...
Fondazione Telethon ETS' Waskyra has become the first gene therapy in the US for patients with Wiskott-Aldrich syndrome (WAS) ...
Based on initial positive results from HOPE-B, etranacogene dezaparvovec became the first gene therapy approved for adults ...
On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...
The Food and Drug Administration this week granted approval to a new gene therapy for a rare immune disorder, the maker of which is notably not a drug ...
The effects allowed these minors who could sit but not stand to move like they've never done before, including walking and ...
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