Camilla served lunch to children from Helen & Douglas House and Roald Dahl's Marvellous Children's Charity during their ...

Samuel Soremekun, aged six, who has sickle cell disease and autism, made everyone laugh when he pointed to a member of her entourage and asked "Is that the King?" ...

Lurie Children's Hospital officially announced an expansion of research with the $11 million from Don and Anne Edwards, who ...

Casgevy safely and effectively prevents vaso-occlusive crises in children ages 5 to 11 with severe sickle cell disease, trial ...

In October 2024, Mercy’s newborn son was diagnosed with sickle cell disease, an inherited blood disorder caused by a mutation ...

Cambridge-based Fulcrum Therapeutics said it will aim to launch a large clinical trial in the second half of 2026 to prove ...

Data presented at ASH suggest that the CRISPR therapy could provide a one-time functional cure in children as young as 5 ...

This year, gene-editing technology was customized to fix mutations in a single patient’s genes for the first time.

Vertex Pharmaceuticals presents clinical data demonstrating benefits of Casgevy in SCD and TDT patients aged 5+ at ASH ...

No maternal deaths and no hydroxyurea-related teratogenic malformations occurred following hydroxyurea exposure during pregnancy in more than 200 patients with sickle cell disease.

Less than a third of ED visits for acute sickle cell disease pain were guideline-adherent for the timely administration of ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...