Caden Major was born with sickle cell disease – an inherited blood disorder affecting red blood cells. Now at 19 years old, ...

Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...

Public health advocates have renewed calls for stronger public education and decisive policy action to improve awareness, promote early detection, expand access to care, and ensure sustained blood ...

Guideline adherence for opioid pain medications was found to be suboptimal among patients with sickle cell disease pain in the ED.

We're living in a moment where science fiction is becoming medical reality. Imagine a world where doctors can simply rewrite ...

In the big picture, matched sibling donor transplants remain the standard of care, Boelens said. But gene therapy is ...

The Founder and Chief Executive Officer of CrimsonBow, Ms Timi Edwin, gave the commendation at the initiative’s ...

Lurie Children's Hospital officially announced an expansion of research with the $11 million from Don and Anne Edwards, who ...

Casgevy safely and effectively prevents vaso-occlusive crises in children ages 5 to 11 with severe sickle cell disease, trial ...

In October 2024, Mercy’s newborn son was diagnosed with sickle cell disease, an inherited blood disorder caused by a mutation ...

Cambridge-based Fulcrum Therapeutics said it will aim to launch a large clinical trial in the second half of 2026 to prove ...

Data presented at ASH suggest that the CRISPR therapy could provide a one-time functional cure in children as young as 5 ...