In Wiskott-Aldrich syndrome trials, therapy was associated with decreases in bleeding, inf ...

ORLANDO -- A gene therapy that could transform CAR T-cell treatment achieved rapid and potentially durable measurable ...

An experimental gene therapy treatment created at UCLA gave a "bubble girl" born with a rare genetic disorder a new life.

A cutting-edge therapy using base-edited immune cells is offering a major breakthrough for patients with one of the toughest ...

The rate of severe infections decreased from 2 infections to 0.2 infections per PYO after treatment with etuvetidigene autotemcel.

Dr. Teresa Blankmeyer Burke is spending the fall semester in Florianópolis, a city in southern Brazil, to study the ethics of ...

Researchers at the University of Geneva, together with colleagues in Switzerland, France, the United States and Israel, ...

They manage to slow down the progression of Huntington's disease using a gene therapy treatment called AMT 130.

A common cold was enough to kill Cora Oakley. Born in Morristown, New Jersey, with virtually no immune system, Cora was diagnosed with severe combined immunodeficiency, a rare genetic condition that ...

FDA clears first gene therapy for rare disease; Roche’s breast cancer pill win; Women increasingly turn to GLP-1s.

Abeona Therapeutics Inc. (Nasdaq: ABEO) today announced activation of The University of Texas Medical Branch (UTMB) in ...

Troy Wichterman, Chief Financial Officer of BioLife Solutions ( BLFS +0.08%), directly sold 30,000 shares on Dec. 4, for a ...